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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
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Research
August 4, 2016
Deep Brain Stimulation and MECP2
August 1, 2016
Results of Copaxone Open Label Trial
July 26, 2016
The Boys of Rett
July 20, 2016
Ask Dr. Carpenter: Episode 1
June 23, 2016
Funding in the Pursuit of Balance
June 20, 2016
First Impressions
May 24, 2016
Attacking Rett Where it Lives | More Funding Awarded
May 2, 2016
Gene Therapy Might be the Best, and Perhaps Only, Chance at Curing Brain Diseases
April 29, 2016
Clarifying the "Vanderbilt Breakthrough Story"
April 19, 2016
“Disease in a Dish” Platform Receives a $1 Million Influx from RSRT
March 31, 2016
Educating the FDA on Breathing Problems
March 15, 2016
Rett Syndrome Clinic in Atlanta Launches Clinical Trial
March 8, 2016
$9 Million Awarded to Research
February 3, 2016
Rett in Review: Crossing Thresholds
January 25, 2016
KCC2 and Rett: The Import/Export Business
January 11, 2016
The Growing Toolbox of Rett Mouse Models
January 5, 2016
Rett Researchers Gather in Boston
December 23, 2015
MECP2 Consortium Progress Report
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40M
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