Talk To Your Doctors
November 14, 2018
If your daughter (or son) is approaching 18 years old, there are a couple of matters that you must handle. While most people know that when our children turn 18 years of age, they are no longer ours, but they are their own person. For me, that meant working with…
What Does it Take to Run a Clinical Trial?
November 6, 2018
Ever wondered how easy or hard it might be to run a clinical trial, or what researchers have to do to be able to run a study? Here we’ll outline some key differences between an academic study and an FDA-regulated study, and talk about our own ketamine clinical trial planned…
UPDATE: AVXS-201 Gene Therapy for Rett Status
October 31, 2018
The entire Rett community celebrated on May 3 of this year when AveXis formally announced plans to submit the IND application for AVXS-201 for Rett syndrome in late 2018/early 2019. We all then held our breath on May 15 when Novartis purchased AveXis for $8.7 billion, wondering whether Novartis would…
Moving the Needle
October 29, 2018
I have always enjoyed the creative process. In my younger days, I was fond of cooking, which was not always sanctioned as an appropriate activity for a young boy in that era of our society. As I moved forward with my high school education, I had an intense interest in…
Confessions of a Novice Event Planner
October 23, 2018
Let me start by disclosing that I am not an event planner nor am I experienced in the world of fundraising or social advocacy. I am a psychologist, an introvert, a dreamer, a neophyte on social media, and most importantly, I am a mom. Before reaching out to RSRT, I…
The Future is Now
August 7, 2018
The DNA double-helix was first postulated to be the building blocks of life by Watson and Crick in a seminal paper in 1953. Their discovery spawned a revolution in molecular biology in the 65 years that have followed, and led to the understanding of human biology, human disease and our…
We’re in This Together
June 12, 2018
Last March we announced an ambitious goal at RSRT to raise $33 million over three years to support our strategic research plan, Roadmap to a Cure. This is no arbitrary goal. Every dollar correlates with a research budget that aggressively moves the needle on potentially curative approaches. I’m excited and…
