Gene Therapy

A Concise Summary of Gene Therapy Clinical Trials for Rett Syndrome

First Pediatric Patient Dosed in Taysha US Clinical Trial

Taysha Pediatric Gene Therapy Trial Is Open for Enrollment in US

Neurogene Doses First Two Patients in Pediatric US Trial

Taysha Expands Age Eligibility for Canadian Clinical Trial

Taysha Cleared to Dose Second Patient in Gene Therapy Trial

Lutz and Liu Dream Team Awarded $23 Million to Cure Four Rare Diseases: Rett is One of Them

Taysha Gene Therapies Doses First Rett Syndrome Patient

Neurogene Shares Key Information on Gene Therapy Clinical Trial with the Rett Community

Cures for Many Rare Disorders Will Come More Quickly Because of Digital Natural History Studies

Neurogene Receives FDA Approval for Gene Replacement Clinical Trial for Rett Syndrome

What We Accomplished in 2022

Leading the Cure for Rett: In Gene Replacement, There’s No Replacement for RSRT

Neurogene Advances a Rett Gene Replacement Program that Got Its Start at RSRT

Town Hall: When will there be a cure for Rett syndrome?

How RSRT is driving the search for a Rett cure

Cure 360 Webinar Series: Gene Replacement for Rett Syndrome 101

Taysha Gene Therapies Statement on Covid-19 Vaccines