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Clinical Trials
November 6, 2025
Neurogene Doses First Participant in Embolden™ Registrational Trial of NGN-401 for Rett Syndrome
October 2, 2025
Taysha Receives FDA Breakthrough Therapy Designation for TSHA-102
August 12, 2025
Taysha Advances REVEAL Pivotal Trial for Rett Syndrome
June 30, 2025
Neurogene Announces Trial Design for Embolden™ Study of NGN-401 Gene Therapy for Rett Syndrome
April 18, 2025
How Will Cuts to FDA and NIH Impact Gene Therapy Clinical Trials and Rett Syndrome Research?
January 15, 2025
A Review of Gene Therapy Clinical Trials
November 30, 2024
Staying Resolute in Challenging Times
November 21, 2024
With Heavy Hearts
November 18, 2024
Neurogene Releases Update on NGN-401 Clinical Trial High Dose
November 13, 2024
Taysha Releases Financial, Enrollment Update and Community Letter
November 11, 2024
Neurogene Announces Interim Results from Gene Therapy Clinical Trial
August 12, 2024
Stepping Out of The Dark Ages and Into The Data
August 12, 2024
Taysha Rett Program Updates Q2 2024
June 18, 2024
Taysha Announced New Clinical Data from the REVEAL Phase 1/2 Adolescent & Pediatric Trial Evaluating TSHA-102
June 3, 2024
FDA Selects Neurogene Rett Program for START Pilot Program
March 19, 2024
Taysha Rett Program Updates March 2024
March 4, 2024
Neurogene Announces Updates to Pediatric Gene Therapy Clinical Trial
February 29, 2024
Taysha Provides Updates for all their Clinical Trials (CAN, US, UK)
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