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Cures
Roadmap to Cures
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Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
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RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
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Rett Fact Cards
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Get Started Now
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Gene Replacement
September 23, 2021
Taysha Gene Therapies Announces Age Range For First Trial During Educational Rett Event for Investors
September 2, 2021
News from Taysha That We are One Step Closer to Testing Gene Replacement for Rett
July 29, 2021
A Reason to Celebrate: Children with a Severe Neurological Disorder Improve After Gene Replacement
July 8, 2021
Gene Replacement for Rett Syndrome 101
June 30, 2021
Cure 360 Webinar Series: Gene Replacement for Rett Syndrome 101
June 3, 2021
In their own words - members of RSRT’s newly formed Translational Medicine Advisory Board share their reasons for optimism
May 26, 2021
Seven New RSRT-Supported Therapeutics Make Their Way Towards Clinical Trials
September 9, 2020
The Next Phase of Our Attack on Rett: CURE 360
December 6, 2016
Gene Editing Shows Potential for Treating Genetic Diseases Like Rett
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