Every question you have ever had about gene replacement for Rett syndrome is asked and answered in this webinar from the Rett Syndrome Research Trust (RSRT). How are genes made in a lab? How do you get the new gene into the body? Is gene replacement really one and done? What have we learned from animal studies? What is the risk associated with gene replacement? Is a cure even possible? Our guest presenter, Dr. Stuart Cobb, first published on Rett as co-author with Adrian Bird on the 2007 reversal paper.
Our Plan for a Cure: Gene Replacement