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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
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Breathing
July 19, 2023
Understanding Rett through the Power of Artificial Intelligence
August 10, 2022
Rett Symptoms in Mice Alleviated with RNA Editing
September 3, 2021
First-Ever Rett Clinical Guidelines Help Us Anticipate Health Changes and Needs
August 14, 2019
Biosensors and the Future of Rett Therapeutics
March 13, 2019
Ketamine Clinical Trial for Rett Syndrome Launches
March 31, 2016
Educating the FDA on Breathing Problems
June 24, 2015
RSRT Awards $530,000 to Neurolixis for Clinical Development of NLX-101
February 6, 2015
RSRT Awards $5.8 Million For Research and Two Clinical Trials
March 17, 2010
Scoliosis in Rett Syndrome
$
40M
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