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Roadmap to Cures
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Research
March 13, 2023
Cures for Many Rare Disorders Will Come More Quickly Because of Digital Natural History Studies
March 7, 2023
Using Cerebral Organoids to Develop MECP2-Activating Drugs for Rett Syndrome
March 3, 2023
What Wearables and AI Can Tell Us About Rett Syndrome Severity
February 9, 2023
New Study Demonstrates MECP2 Reactivation
February 1, 2023
Taysha Provides Update For Their Rett Syndrome Gene Replacement Program
January 23, 2023
Neurogene Receives FDA Approval for Gene Replacement Clinical Trial for Rett Syndrome
January 10, 2023
The Story Behind Mini-MeCP2
December 19, 2022
What We Accomplished in 2022
December 13, 2022
What We Learned from Taysha’s Clinical Trial Community Update
December 7, 2022
Why Biosensors Will Revolutionize How Treatments Are Evaluated
November 29, 2022
Leading the Cure for Rett: In Gene Replacement, There’s No Replacement for RSRT
November 10, 2022
What do astronauts and people living with Rett have in common?
October 26, 2022
Taysha Gene Therapies Shares Rett Syndrome Community Statement on its Collaboration with Astellas Gene Therapies
October 25, 2022
Taysha Announces Collaboration with Astellas Gene Therapies
September 29, 2022
Results of the Rett ORCA Study: How Rett Families Are Impacting Clinical Trials
August 25, 2022
RNA Editing and Its Potential to Improve Rett Syndrome Symptoms
August 10, 2022
Rett Symptoms in Mice Alleviated with RNA Editing
July 1, 2022
A Conversation with Neurogene's Leadership
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