Research

Taysha Reports on Patient #1

RSRT Doubles Down on RNA Editing for Rett Syndrome with Additional Funding to Beal Lab at UC Davis

Taysha Cleared to Dose Second Patient in Gene Therapy Trial

Understanding Rett through the Power of Artificial Intelligence

Neurogene Merges with Neoleukin

Lutz and Liu Dream Team Awarded $23 Million to Cure Four Rare Diseases: Rett is One of Them

Details on Neurogene Gene Therapy Trial Now on ClinicalTrial.gov

Taysha Gene Therapies Doses First Rett Syndrome Patient

"There are no 'crazy experiments' when it comes to Rett"

Neurogene Shares Key Information on Gene Therapy Clinical Trial with the Rett Community

An Update on the New Rett Digital Natural History Study: How Our Children’s Medical Records Created a Decades-Long Study in Months

DAYBUE (trofinetide): Key Facts for Parents

Cures for Many Rare Disorders Will Come More Quickly Because of Digital Natural History Studies

Using Cerebral Organoids to Develop MECP2-Activating Drugs for Rett Syndrome

What Wearables and AI Can Tell Us About Rett Syndrome Severity

New Study Demonstrates MECP2 Reactivation

Taysha Provides Update For Their Rett Syndrome Gene Replacement Program

Neurogene Receives FDA Approval for Gene Replacement Clinical Trial for Rett Syndrome