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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
Rett Clinics & Clinical Trials
Thriving with Rett Guides
Rett Fact Cards
Researchers
Fundraise
Get Started Now
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Drug Discovery
May 19, 2023
"There are no 'crazy experiments' when it comes to Rett"
April 14, 2022
Town Hall: When will there be a cure for Rett syndrome?
September 21, 2021
A Company working on a Rett Curative Therapy is Getting Backed by a Pharmaceutical Powerhouse
June 19, 2017
Precision Medicine
September 10, 2014
Guest Blogger: Drug Therapies and Rett
December 11, 2012
Who’s In Charge?
June 2, 2011
Rett Syndrome: Neurodevelopmental No Longer
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40M
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