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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
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Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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For All Families
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Get Started Now
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Research
July 12, 2017
What About Us?
June 19, 2017
Precision Medicine
June 8, 2017
AveXis Announcement - Delivering on Roadmap to a Cure
May 15, 2017
Gene Therapy Consortium Reports on Progress
May 10, 2017
Gene Therapy Primer
April 25, 2017
Racing Down The Gene Therapy Highway To A Cure
March 30, 2017
Orphan Drug Designation: What Does it Mean?
March 27, 2017
New Insight Into MECP2 Mutation Hotspot
March 24, 2017
Roadmap to a Cure FAQ
March 17, 2017
RSRT Awards $7.5 Million to Research in 2016
February 28, 2017
Key Questions to Ask When Considering Clinical Trials
February 2, 2017
Awaken and Activate the Mighty X Chromosome
January 27, 2017
Of Mice and Rett: Novel Therapeutics & Community Support
December 14, 2016
Rare Disease Drug Approval Sparks Controversy
December 6, 2016
Gene Editing Shows Potential for Treating Genetic Diseases Like Rett
September 27, 2016
What the Chan Zuckerberg Initiative Means for Rett Research
August 18, 2016
Mortgaging the House
August 10, 2016
Deep Brain Stimulation: Next Steps
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