Curing Rett Syndrome – How Do We Get There?
Executive Director of RSRT
Monica gives an overview of the various approaches from gene therapy to drug screens and everything in between that are being pursued to cure Rett Syndrome. We encourage you to invest 30 minutes of your time and arm yourselves with the facts.
Gene Awakenings for the Treatment of Neurological Disorders
Ben Philpot, Ph.D.
University of North Carolina at Chapel Hill
Late last year RSRT made a $2.2 million investment in the labs of Ben Philpot and his colleagues to conduct a screen to identify compounds that can unsilence a healthy copy of the mutated Rett gene. The screen is now up and running. Learn the basics of how the screen works and why we are optimistic about this approach.