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Cures
Roadmap to Cures
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Roadmap 1.0
Delivery
Viral
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Small RNA
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Research
February 25, 2020
The Launch of a New Partnership
January 28, 2020
Can Food be Medicine?
January 13, 2020
New Insight Into How MeCP2 Regulates Transcription
November 30, 2019
Prime Time
August 22, 2019
AveXis/Novartis Release Statement on AVXS-201
August 14, 2019
Biosensors and the Future of Rett Therapeutics
August 10, 2019
Harnessing Exosomes as a Therapeutic for Rett Syndrome
August 2, 2019
New Drugs Restore Brain Balance to Treat Rett Syndrome
July 3, 2019
My First 9 Months at RSRT
June 5, 2019
Making Sense of it All
June 1, 2019
A Big Step for Gene Therapy
March 13, 2019
Ketamine Clinical Trial for Rett Syndrome Launches
January 24, 2019
On the Shoulders of Giants
January 14, 2019
What’s Making MeCP2 Toxic in Duplication Syndrome?
December 13, 2018
World-Class Team Takes on Next Gen Gene Therapy
November 19, 2018
New Method Developed to Study MeCP2 Function in Humans
November 6, 2018
What Does it Take to Run a Clinical Trial?
October 31, 2018
UPDATE: AVXS-201 Gene Therapy for Rett Status
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