Rett Syndrome Genetic Medicines Summit 2023
In 2023 we hosted the first meeting of its kind with biopharma companies front and center. The Summit gathered basic scientists, pre-clinical, clinical, and regulatory experts to foster discussion, refine expectations, and identify best practices to expedite genetic medicine development.
Featured Speakers
Summit Program Book
RSRT invited 130 scientists and clinicians from 20 academic institutions, 43 biopharmaceutical companies, NIH and FDA to participate at the Summit via presentations, panel discussions and poster session.
In Their Own Words
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The 2025 Summit
Over the course of three days in September we convened leading scientists, clinicians, and regulators to explore every corner of the genetic medicines landscape. The leadership from over 45 biopharma companies had a unique opportunity to hear about the state of Rett genetic medicine programs, with the ultimate goal of inspiring and motivating them to add the disorder to their pipelines.
This year’s gathering underscored RSRT’s role as both convener and catalyst, bringing brilliant minds together while never losing sight of the children and families at the heart of our community.
"RSRT has done an incredible job. The number of modalities and the caliber of intellect in the room is off the charts high. These are the top people in their fields and they're interested in Rett syndrome. That's not easy to do."
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