While we fervently hope that the AveXis trial delivers significant and dramatic results we suspect there will be room for improvement. Fortunately, technological advances in gene therapy are happening quickly with more effective vectors being discovered that can carry larger DNA cargos and target a greater percentage of brain cells.
World-Class Team Takes on Next Gen Gene Therapy
In late 2018 RSRT announced a Gene Therapy Consortium 2.0 comprised of a world-class team. The goal will be to have a next generation gene therapy product…should we need it.. ready for clinical testing by 2021.